The United States of America; as Represented by the Secretary of the Department of Health and Human
发明人:
John Fitzgerald Tisdale,Bjorg Gudmundsdottir,Laxminath Tumburu
申请号：
US16676369
公开号：
US20200216545A1
申请日:
2019.11.06
申请国别(地区):
US
年份:
2020
代理人:
摘要：
The present invention provides new compositions and methods useful for the treatment and potential cure of beta-globinopathies such as sickle cell disease and beta-thalassemia by inhibiting the expression and/or activity of RIOK3.
