EFFECTIVE SYSTEMIC TREATMENT OF DYSTROPHIC PATHOLOGIES

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专利权人:

Royal Holloway And Bedford New College;GENETHON

发明人:

DICKSON, George,Voit, Thomas,MOULLIER, Philippe,LE GUINER, Caroline

申请号：

DK15731377

公开号：

DK3044319T3

申请日:

2015.06.29

申请国别(地区):

DK

年份:

2018

代理人:

摘要：

A composition comprising a gene therapy product for use in the treatment of a dystrophic disease in a subject, advantageously in humans, wherein: - the gene therapy product comprises a nucleic acid sequence encoding a functional microdystrophin； - the composition is systemically administered.

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中国工程科技知识中心

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http://www.ckcest.cn/home/