Michalakis, Stylianos,Biel, Martin,Seeliger, Mathias,Schoen, Christian
申请号:
AU2017222231
公开号:
AU2017222231A1
申请日:
2017.02.23
申请国别(地区):
AU
年份:
2018
代理人:
摘要:
The present invention relates to a polynucleotide configured for the treatment of a retinal degeneration disease, such as retinitis pigmentosa (RP), a nucleic acid vector comprising said polynucleotide, a pharmaceutical composition comprising said nucleic acid vector, a kit comprising said polynucleotide or said nucleic acid vector, a method of making said nucleic acid vector, and a method for treating a retinal degeneration disease.