The United States of America;as represented by the Secretary;Department of Health and Human Services
发明人:
Zhijian Wu,Anand Swaroop,Suja Hiriyanna,Tiansen Li
申请号：
US16854605
公开号：
US20200289670A1
申请日:
2020.04.21
申请国别(地区):
US
年份:
2020
代理人:
摘要：
Disclosed are adeno-associated virus (AAV) vectors comprising a nucleotide sequence encoding RP2 or RPGR-ORF15 and related pharmaceutical compositions. Also disclosed are methods of treating or preventing X-linked retinitis pigmentosa, increasing photoreceptor number in a retina of a mammal, and increasing visual acuity of a mammal using the vectors and pharmaceutical compositions.
