Bennett, C. Frank,Rigo, Frank,Cleveland, Don W.,Lagier-Tourenne, Clotilde,Ravits, John M.,Baughn, Michael W.
申请号:
AU2014337506
公开号:
AU2014337506A1
申请日:
2014.10.14
申请国别(地区):
AU
年份:
2016
代理人:
摘要:
Disclosed herein are methods for reducing expression of C90RF72 antisense transcript in an animal with C90RF72 antisense transcript specific inhibitors. Such methods are useful to treat, prevent, or ameliorate neurodegenerative diseases in an individual in need thereof. Such C90RF72 antisense transcript specific inhibitors include antisense compounds.