Compositions for modulating expression of C9ORF72 antisense transcript

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专利权人:

Ionis Pharmaceuticals; Inc.

发明人:

Frank Rigo

申请号：

US15565838

公开号：

US10407678B2

申请日:

2015.04.16

申请国别(地区):

US

年份:

2019

代理人:

摘要：

Disclosed herein are compositions and methods for modulating expression of C9ORF72 antisense transcript in a cell or animal with C9ORF72 antisense transcript specific inhibitors. Such methods are useful to treat, prevent, or ameliorate neurodegenerative diseases in an individual in need thereof. Such C9ORF72 antisense transcript specific inhibitors include antisense compounds.

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