UNIVERSITE PARIS-SUD XI;INSERM (INSTITUT NATIONAL DE LA SANTE ET DE LA RECHERCHE MEDICALE);UNIVERSITE DE STRASBOURG;CENTRE NATIONAL DE LA RECHERCHE SCIENTIFIQUE ( CNRS);HELENE MONIQUE PUCCIO;PATRICK A
发明人:
申请号：
IL24031115
公开号：
IL240311D0
申请日:
2015.08.02
申请国别(地区):
IL
年份:
2015
代理人:
摘要：
A method for preventing or treating cardiomyopathy due to energy failure in a subject in need thereof is provided. The method comprises administering to the subject a therapeutically effective amount of a vector which comprises a nucleic acid sequence encoding a gene that can reverse energy failure. An exemplary cardiomyopathy is that which is associated with Friedreich ataxia and an exemplary nucleic acid sequence comprises a nucleic acid that encodes frataxin (FXN).
