Compositions and methods for treating succinic semialdehyde dehydrogenase deficiency (SSADHD)

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专利权人:

Washington State University

发明人:

VOGEL, Kara Rain,GIBSON, Kenneth Michael,AINSLIE, Garrett Robert

申请号：

AU2019225729

公开号：

AU2019225729A1

申请日:

2019.02.12

申请国别(地区):

AU

年份:

2020

代理人:

摘要：

Provided herein are compositions and methods for treating succinic semialdehyde dehydrogenase deficiency (SSADHD). Compositions may include a gene encoding a functional succinic semialdehyde dehydrogenase (SSADH) enzyme, such as

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中国工程科技知识中心

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