Methods for preventing and/or treating lysosomal storage disorders

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专利权人:

Inc.;Amicus Therapeutics

发明人:

Boyd, Robert,Lee, Gary

申请号：

AU2010233188

公开号：

AU2010233188B2

申请日:

2010.04.09

申请国别(地区):

AU

年份:

2015

代理人:

摘要：

The present invention provides methods for preventing and/or treating lysosomal storage disorders using 5-(fluoromethyl)piperdine-3,4-diol, 5- (chloromethyl)piperdine-3,4-diol, or a pharmaceutically acceptable salt, solvate, or prodrug thereof, or any combination of two or more thereof. In particular, the present invention provides methods for preventing and/or treating Gaucher's disease.

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中国工程科技知识中心

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http://www.ckcest.cn/home/