APPEL, LEAH E.,SHOCKEY, JOSHUA R.,SCHELLING, D. CHRISTOPHER
申请号：
CA3017573
公开号：
CA3017573A1
申请日:
2016.10.17
申请国别(地区):
CA
年份:
2017
代理人:
摘要：
The present invention features palatable pharmaceutical compositions including sodium phenylbutyrate and methods for the treatment of inborn errors of metabolism (e.g., Maple Syrup Urine Disease or Urea Cycle Disorders), neurodegenerative disorders such as Parkinson's disease, spinal muscular atrophy, dystonia, or inclusion-body myositis with such compositions.
