Appel, Leah E.,Shockey, Joshoua R.,Schelling, D. Christopher
申请号：
AU2016398029
公开号：
AU2016398029A1
申请日:
2016.10.17
申请国别(地区):
AU
年份:
2018
代理人:
摘要：
The present invention features palatable pharmaceutical compositions including sodium phenylbutyrate and methods for the treatment of inborn errors of metabolism (e.g., Maple Syrup Urine Disease or Urea Cycle Disorders), neurodegenerative disorders such as Parkinsons disease, spinal muscular atrophy, dystonia, or inclusion-body myositis with such compositions.
