COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
- 专利权人:
- Sarepta Therapeutics; Inc.
- 发明人:
- Edward M. KAYE
- 申请号：
- US16422241
- 公开号：
- US20190359982A1
- 申请日:
- 2019.05.24
- 申请国别(地区):
- US
- 年份:
- 2019
- 代理人:
- 摘要：
- Improved compositions and methods for treating muscular dystrophy by administering antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon skipping are described.
- 来源网站：
- 中国工程科技知识中心
