FLANIGAN KEVIN,VULIN-CHAFFIOL ADELINE,WEIN NICOLAS
申请号：
IN3577/KOLNP/2015
公开号：
IN2015KN03577A
申请日:
2015.10.28
申请国别(地区):
IN
年份:
2016
代理人:
摘要：
The present invention relates to recombinant adeno-associated virus (rAAV) delivery of polynucleotides for treating Duchenne Muscular Dystrophy resulting from the duplication of DMD exon 2. The invention provides rAAV products and methods of using the rAAV in the treatment of Duchenne Muscular Dystrophy.
