ADENO-ASSOCIATED VIRUS FACTOR VIII VECTORS, ASSOCIATED VIRAL PARTICLES AND THERAPEUTIC FORMULATIONS COMPRISING THE SAME

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专利权人:

发明人:

BUNTING STUART,COLOSI PETER CAMERON,PUNGOR ERNO

申请号：

IN201817012485

公开号：

IN201817012485A

申请日:

2018.04.02

申请国别(地区):

IN

年份:

2018

代理人:

摘要：

The invention provides adeno-associated virus (AAV) Factor VIII (FVIII)- encoding/expressing vectors and virus, including AAV FVIII vectors with high expression activity and AAV FVIII vectors that express full-length or truncated functional FVIII protein. The invention also relates to methods of making the herein described AAV FVIII vectors, recombinant AAV FVIII virus particles comprising or expressing such vectors, associated pharmaceutical formulations comprising the same and therapeutic uses thereof.

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中国工程科技知识中心

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http://www.ckcest.cn/home/