GASMI, Mehdi,CRYSTAL, Ronald G.,PAGOVICH, Odelya E.
申请号：
EP17835222
公开号：
EP3490613A4
申请日:
2017.07.26
申请国别(地区):
EP
年份:
2020
代理人:
摘要：
A vector comprising a promoter operably linked to a nucleic acid sequence encoding human aldehyde dehydrogenase, as well as a composition comprising the vector and method of using the vector to treat aldehyde dehydrogenase deficiency, or to prevent or treat a disease characterized by aldehyde dehydrogenase deficiency.
