MICHAEL HEARTLEIN,BRAYDON, CHARLES GUILD,FRANK DEROSA,CARSTEN RUDOLPH,CHRISTIAN PLANK,LIANNE SMITH
申请号:
PT14718284
公开号:
PT2968586T
申请日:
2014.03.14
申请国别(地区):
PT
年份:
2018
代理人:
摘要:
Materials, formulations, production methods, and methods for delivery of CFTR mRNA for induction of CFTR expression, including in the mammalian lung are provided. The present invention is particularly useful for treating cystic fibrosis.