METHODS FOR TREATING DANONE DISEASE AND OTHER AUTOFAGIA DISORDERS

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专利权人:

发明人:

申请号：

RU2018129975

公开号：

RU2018129975A3

申请日:

申请国别(地区):

RU

年份:

2020

代理人:

摘要：

This disclosure provides gene therapy vectors comprising a polynucleotide encoding one or more isoforms of lysosome-associated membrane protein 2 (LAMP-2), and methods of using such gene therapy vectors for the treatment of Danon disease and other autophagy disorders.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/