用於治療杜興型肌營養不良症和貝克型肌營養不良症的具有改善特性的RNA調節性寡核苷酸
- 专利权人:
- BIOMARIN TECHNOLOGIES B.V.
- 发明人:
- PETER CHRISTIAN DE VISSER,JUDITH CHRISTINA THEODORA VAN DEUTEKOM
- 申请号：
- HK15104532.0
- 公开号：
- HK1203835A
- 申请日:
- 2015.05.13
- 申请国别(地区):
- HK
- 年份:
- 2015
- 代理人:
- 摘要：
- The current invention provides an improved oligonucleotide and its use for treating, ameliorating, preventing and/or delaying DMD or BMD.
- 来源网站：
- 中国工程科技知识中心
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相关专利
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- A SPECIFIC GENE RELATED TO RESPIRATORY DISEASE, DOUBLE-DESIGNED OLIGO-RNA CONSTRUCTION CONTAINING miRNA, AND CONTAINING ITS COMPOSITION FOR PREVENTION OR TREATMENT
