SiRNA therapy for transthyretin (TTR) related ocular amyloidosis

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专利权人:

Alnylam Pharmaceuticals, Inc.;Hirofumi Jono;Yukio Ando;Kumamoto University

发明人:

Ando, Yukio,Jono, Hirofumi,Alvarez, Rene,Sah, Dinah Wen-Yee

申请号：

AU2011235276

公开号：

AU2011235276A1

申请日:

2011.03.29

申请国别(地区):

AU

年份:

2012

代理人:

摘要：

The invention relates to a method of treating ocular amyloidosis by reducing TTR expression in a subject by administering a double-stranded ribonucleic acid (dsRNA) that targets a TTR gene to the retinal pigment epithelium of the subject.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/