COMPOSITIONS AND METHODS FOR GENE EDITING FOR HEMOPHILIA A

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专利权人:

Casebia Therapeutics Limited Liability Partnership

发明人:

Alan Richard BROOKS

申请号：

US16163536

公开号：

US20190247517A1

申请日:

2018.10.17

申请国别(地区):

US

年份:

2019

代理人:

摘要：

Provided include materials and methods for treating Hemophilia A in a subject ex vivo or in vivo. Also provided include materials and methods for knocking in a FVIII-encoding gene in a genome, in particular the locus of albumin gene.

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中国工程科技知识中心

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http://www.ckcest.cn/home/