POLYNUCLEOTIDE AGENTS TARGETING SERPINC1 (AT3) AND METHODS OF USE THEREOF
- 专利权人:
- 发明人:
- 申请号:
- EP15795074.2
- 公开号:
- EP3212794A2
- 申请日:
- 2015.10.28
- 申请国别(地区):
- EP
- 年份:
- 2017
- 代理人:
- 摘要:
- The invention relates to polynucleotide agents targeting the Serpinc1 (AT3) gene, and methods of using such polynucleotide agents to inhibit expression of Serpinc1 and to treat subjects having a bleeding disorder, e.g., a hemophilia.
- 来源网站:
- 中国工程科技知识中心
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