GARRIT-JAN BOUDEWIJN VAN OMMEN,JOSEPHUS JOHANNES DE KIMPE,JUDITH CHRISTINA THEODORA VAN DEUTEKOM,ANNEMIEKE AARTSMA-RUS,GERARD JOHANNES PLATENBURG
申请号：
PT14179979
公开号：
PT2813570T
申请日:
2009.05.14
申请国别(地区):
PT
年份:
2018
代理人:
摘要：
The invention provides a method for modulating skipping of Duchenne Muscular Dystrophy (DMD) gene in a cell. More specifically, the invention provides methods and means for modulating skipping of exon 44 of DMD. The invention further provides nucleic acid molecules that can be used for a method of the invention, expression methods for expression of a nucleic acid molecule in a cell, and use of a nucleic acid molecule for modulating skipping of DMD in a cell.
