COMPOSIÇÕES PARA MODULAR A EXPRESSÃO DE C9ORF72

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专利权人:

IONIS PHARMACEUTICALS; INC.

发明人:

申请号：

PT16780833

公开号：

PT3283080T

申请日:

2016.04.15

申请国别(地区):

PT

年份:

2020

代理人:

摘要：

Disclosed herein are compositions and methods for reducing expression of C9ORF72 mRNA and protein in an animal. Such methods are useful to treat, prevent, ameliorate, or slow progression of neurodegenerative diseases in an individual in need thereof.

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中国工程科技知识中心

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http://www.ckcest.cn/home/