LABORATORIOS DEL DR. ESTEVE S.A.;UNIVERSITAT AUTÓNOMA DE BARCELONA
发明人:
Maria Fàtima BOSCH TUBERT,Virginia AREBA HAURIGOT,Sandra MOTAS MALLOL
申请号：
US15578366
公开号：
US20180169272A1
申请日:
2016.06.03
申请国别(地区):
US
年份:
2018
代理人:
摘要：
The present invention provides new Adeno-associated virus-derived vectors and pharmaceutical compositions containing the same for the treatment of lysosomal storage disorders and specially, for the treatment of mucopolysaccharidoses Type II.
