Development of targeted therapies for peroxisome biogenesis disorders

负责人：

关键词：

PEX1 Molecular Biology peroxisome biogenesis disorders peroxins high-content screening small molecules induced pluripotent stem cells HepG2 cells Pex1-p.G844D mouse

DOI：

doi:10.25549/usctheses-c40-298640

摘要：

of the derived cells. We also generated and characterized HepG2 PEX1 mutant cell lines with peroxisome assembly defects. Finally, I also participated