Alnylam Pharmaceuticals, Inc.;Icahn School of Medicine at Mount Sinai
发明人:
BETTENCOURT, Brian,FITZGERALD, Kevin,QUERBES, William,YASUDA, Makiko,DESNICK, Robert J.
申请号:
HK18110394
公开号:
HK1251014A1
申请日:
2018.08.14
申请国别(地区):
HK
年份:
2019
代理人:
摘要:
The invention relates to double-stranded ribonucleic acid (dsRNA) compositions targeting the ALAS1 gene, and methods of using such dsRNA compositions to alter (e.g., inhibit) expression of ALAS1.