DE VISSER PETER CHRISTIAN,VAN DEUTEKOM JUDITH CHRISTINA THEODORA
申请号：
NZ62789613
公开号：
NZ627896A
申请日:
2013.01.28
申请国别(地区):
NZ
年份:
2016
代理人:
摘要：
Discloses an oligonucleotide comprising a 2&rsquo； -O-methyl RNA monomer and a phosphorothioate backbone and comprising a 5-methyluracil and/or a 5-methylcytosine and/or a 2,6-diaminopurine base for use in the treatment of Duchenne Muscular Dystrophy or Becker Muscular Dystrophy.
