KOMPOZICIJOS IR BŪDAI, SKIRTI SMN2 SPLAISINGO MODULIAVIMUI

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专利权人:

Biogen MA Inc.;COLD SPRING HARBOR LABORATORY

发明人:

BAKER, Brenda F.,KRAINER, Adrian R.,HUA, Yimin

申请号：

LT17185196

公开号：

LT3308788T

申请日:

2006.06.23

申请国别(地区):

LT

年份:

2018

代理人:

摘要：

Disclosed herein are compounds, compositions and methods for modulating splicing of SMN2 mRNA in a cell, tissue or animal. Also provided are uses of disclosed compounds and compositions in the manufacture of a medicament for treatment of diseases and disorders, including spinal muscular atrophy.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/