The Children's Hospital of Philadelphia;The Childrens Hospital of Philadelphia
发明人:
Davidson, Beverly L.,Monteys, Alejandro Mas,Keiser, Megan S.
申请号:
AU2017234929
公开号:
AU2017234929A1
申请日:
2017.03.17
申请国别(地区):
AU
年份:
2018
代理人:
摘要:
The present disclosure provides filler or stuffer sequences, compositions thereof including expression cassettes and vectors, such as viral (e.g., AAV) vectors and methods of delivering a therapeutic agent to a mammal and/or treating a disease.