The United States of America; as represented by The Secretary; Department of Health and Human Services
发明人:
申请号：
EP20176667.2
公开号：
EP3719134A1
申请日:
2016.03.11
申请国别(地区):
EP
年份:
2020
代理人:
摘要：
Disclosed are adeno-associated virus (AAV) vectors comprising a nucleotide sequence encoding RP2 or RPGR-ORF15 and related pharmaceutical compositions. Also disclosed are methods of treating or preventing X-linked retinitis pigmentosa, increasing photoreceptor number in a retina of a mammal, and increasing visual acuity of a mammal using the vectors and pharmaceutical compositions.
