The McLean Hospital Corporation; Inc.;Shire Human Genetic Therapies;Shire Human Genetic Therapies, Inc.
发明人:
Park, Yung Hee,Isacson, Ole
申请号：
AU2016256895
公开号：
AU2016256895A1
申请日:
2016.05.06
申请国别(地区):
AU
年份:
2017
代理人:
摘要：
The present invention is directed, in part, to the treatment of a subject having a neurodegenerative disorder, such as Parkinson's disease (PD), by providing glucocerebrosidase enzyme. The enzyme may be provided, e.g., through gene therapy or by administration of a glucocerebrosidase protein. Accordingly, the present invention encompasses glucocerebrosidase nucleic acids or proteins for use in the treatment of PD or other neurodegenerative disorders.
