BIOMARIN PHARMACEUTICAL INC.;UNIVERSITY COLLEGE LONDON
发明人:
COLOSI, PETER, CAMERON,NATHWANI, AMIT,MCINTOSH, JENNY,TUDDENHAM, EDWARD
申请号:
SG11201601932U
公开号:
SG11201601932UA
申请日:
2014.09.10
申请国别(地区):
SG
年份:
2016
代理人:
摘要:
The invention provides improved adeno-associated virus (AAV) Factor VIII (FVIII) vectors, including AAV FVIII vectors that produce a functional Factor VIII polypeptide and AAV FVIII vectors with high expression activity.