שיטות ותכשירים לטיפול במחלות נדירות

• 收藏
• 分享

专利权人:

SANGAMO THERAPEUTICS INC.

发明人:

申请号：

IL27395920

公开号：

IL273959D0

申请日:

2020.04.13

申请国别(地区):

IL

年份:

2020

代理人:

摘要：

The present disclosure is in the field of modulation of genes involved in rare diseases including for diagnostics and therapeutics for rare diseases such as Angelman's Syndrome, Facioscapulohumeral Muscular Dystrophy (FHMD), Amyotrophic Lateral Sclerosis (ALS), Frontotemporal dementia (FTD) and Spinal Muscular Atrophy (SMA).

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/