John M. McCall;Matthew Robert Johnson;Jill Heemskerk;Graham Johnson;Keith D. Barnes;David Fairfax
发明人:
Jill Heemskerk,Keith D. Barnes,John M. McCall,Graham Johnson,David Fairfax,Matthew Robert Johnson
申请号:
US13310965
公开号:
US20120083495A1
申请日:
2011.12.05
申请国别(地区):
US
年份:
2012
代理人:
摘要:
Compounds useful for the treatment of spinal muscular atrophy or other uses, as well as methods of using such compounds to increase SMN expression, increase EAAT2 expression, or increase the expression of a nucleic acid that encodes a translational stop codon introduced by mutation or frameshift.