BIOMARIN PHARMACEUTICAL INC.;UNIVERSITY COLLEGE LONDON
发明人:
COLOSI, PETER, CAMERON,NATHWANI, AMIT,MCINTOSH, JENNY,TUDDENHAM, EDWARD
申请号：
PH12016500328
公开号：
PH12016500328A1
申请日:
2016.02.18
申请国别(地区):
PH
年份:
2016
代理人:
摘要：
The invention provides improved adeno-associated virus (AAV) Factor VIII (FVIII) vectors, including AAV FVIII vectors that produce a functional Factor VIII polypeptide and AAV FVIII vectors with high expression activity.
