Alfica Sehgal,Klaus Charisse,Brian Bettencourt,Martin Maier,Kallanthottathil G. Rajeev,Gregory Hinkle,Muthiah Manoharan
申请号：
US15399820
公开号：
US10030244B2
申请日:
2017.01.06
申请国别(地区):
US
年份:
2018
代理人:
摘要：
The invention relates to RNAi agents, e.g., double-stranded RNAi agents, targeting the Serpina1 gene, and methods of using such RNAi agents to inhibit expression of Serpina1 and methods of treating subjects having a Serpina1 associated disease, such as a liver disorder.
