CHARLES GUILD BRAYDON,FRANK DEROSA,MICHAEL HEARTLEIN,MICHAEL CONCINO
申请号:
PT18156531
公开号:
PT3338765T
申请日:
2010.11.30
申请国别(地区):
PT
年份:
2019
代理人:
摘要:
Disclosed herein are compositions and methods of modulating the expression of gene or the production of a protein by transfecting target cells with nucleic acids. The compositions disclosed herein demonstrate a high transfection efficacy and are capable of ameliorating diseases associated with protein or enzyme deficiencies.