Youhealth Biotech, Limited;The Regents of the University of California
发明人:
申请号:
EP17868171.4
公开号:
EP3534911A4
申请日:
2017.11.03
申请国别(地区):
EP
年份:
2020
代理人:
摘要:
Disclosed herein are methods and pharmaceutical compositions for the treatment of retinitis pigmentosa, macular degeneration and other retinal conditions by interfering with expression of genes, such as those encoding photoreceptor cell-specific nuclear receptor and neural retina-specific leucine zipper protein, in cells of the eye. These methods and compositions employ nucleic acid based therapies.