BRAINVECTIS;INSERM (INSTITUT NATIONAL DE LA SANTË ET DE LA RECHERCHE MÊDICALE);UNIVERSIDADE DE COIMBRA;CENTRO DE NEUROCIÊNCIAS E BIOLOGIA CELULAR
发明人:
Sandro ALVES,Nathalie CARTIER-LACAVE,Luis PEREIRA DE ALMEIDA,Clévio NOBREGA,Liliana MENDONÇA
申请号:
US16480541
公开号:
US20190343927A1
申请日:
2018.01.30
申请国别(地区):
US
年份:
2019
代理人:
摘要:
The present invention relates to a vector for use in the treatment of a polyglutamine repeat spinocerebellar ataxia, which vector comprises cholesterol 24-hydroxylase encoding nucleic acid.