SUHY, DAVID,GRAHAM, MICHAEL,TROLLET, CAPUCINE,MALERBA, ALBERTO,DICKSON, GEORGE J.
申请号：
CA3020754
公开号：
CA3020754A1
申请日:
2017.04.13
申请国别(地区):
CA
年份:
2017
代理人:
摘要：
The present disclosure relates to RNA interference (RNAi) reagents targeting PABPN1 for treatment of oculopharyngeal muscular dystrophy (OPMD), compositions comprising same, and use thereof to treat individuals suffering from OPMD or which are predisposed thereto.
