FUNDACION INSTITUTO DE INVESTIGACION SANITARIA FUNDACION JIMENEZ DIAZ;CONSORCIO CENTRO DE INVESTIGACION BIOMEDICA EN RED ;CENTRO DE INVESTIGACIONES ENERGETICAS MEDIOAMBIENTALES Y TECNOLOGICAS O.A. M.P
发明人:
申请号:
IL27373720
公开号:
IL273737D0
申请日:
2020.04.01
申请国别(地区):
IL
年份:
2020
代理人:
摘要:
The present disclosure provides polynucleotide cassettes, expression vectors and methods for the expression of a gene in mammalian cells to provide gene therapy for pyruvate kinase deficiency.