DREYFUSS, Gideon,WAN, Lili,OH, Jung Min,PINTO, Anna Maria,YOUNIS, Ihab,BERG, Michael
申请号:
ES13813188
公开号:
ES2785274T3
申请日:
2013.07.05
申请国别(地区):
ES
年份:
2020
代理人:
摘要:
The present invention relates to the discovery of a novel global gene expression regulation mechanism whereby U1 snRNP (U1) protects pre-mRNAs. In one embodiment, the invention includes compositions and methods for regulating gene expression and treating diseases associated with dysregulated gene expression.