BioMarin Pharmaceutical Inc.;University College London
发明人:
COLOSI, Peter Cameron,NATHWANI, Amit,MCINTOSH, Jenny,TUDDENHAM, Edward
申请号:
DK14771729
公开号:
DK3044231T3
申请日:
2014.09.10
申请国别(地区):
DK
年份:
2020
代理人:
摘要:
The invention provides improved adeno-associated virus (AAV) Factor VIII (FVIII) vectors, including AAV FVIII vectors that produce a functional Factor VIII polypeptide and AAV FVIII vectors with high expression activity.