Osborn, Mark J.,Tolar, Jakub,Blazar, Bruce,Voytas, Daniel F.
申请号:
AU2020200307
公开号:
AU2020200307A1
申请日:
2020.01.16
申请国别(地区):
AU
年份:
2020
代理人:
摘要:
#$%^&*AU2020200307A120200206.pdf#####ABSTRACT The invention is directed to transcription activator-like effector nuclease (TALEN)-mediated DNA editing of disease-causing mutations in the context of the human genome and human cells to treat patients with compromised genetic disorders.