Kallanthottathil G. Rajeev,Tracy Zimmermann,Muthiah Manoharan,Martin A. Maier,Satyanarayana Kuchimanchi,Klaus Charisse
申请号:
US16738014
公开号:
US20200318111A1
申请日:
2020.01.09
申请国别(地区):
US
年份:
2020
代理人:
摘要:
The present invention provides RNAi agents, e.g., double stranded RNAi agents, that target the transthyretin (TTR) gene and methods of using such RNAi agents for treating or preventing TTR-associated diseases.