GROSSMAN, TAMAR R.,FREIER, SUSAN M.,MINASSIAN, BERGE,AHONEN, SAIJA
申请号:
CA3023514
公开号:
CA3023514A1
申请日:
2017.06.19
申请国别(地区):
CA
年份:
2017
代理人:
摘要:
Provided herein are methods, compounds, and compositions for reducing expression of GYS1 in an individual. Such methods, compounds, and compositions are useful to treat, prevent, delay, or ameliorate a glycogen storage disease or disorder in an individual in need.