Nippon Shinyaku Co.;National Center of Neurology and Psychiatry; Ltd.;Nippon Shinyaku Co., Ltd.
发明人:
申请号:
EP15761392.8
公开号:
EP3118311B1
申请日:
2015.03.11
申请国别(地区):
EP
年份:
2018
代理人:
摘要:
Provided is a drug that allows highly-efficient skipping of exon 51 in the human dystrophin gene. The present invention provides an antisense oligomer which enables exon 51 in the human dystrophin gene to be skipped.