GEORG-AUGUST-UNIVERSITAT GOTTINGEN STIFTUNG OFFENTLICHEN RECHTS, UNIVERSITATSMEDIZIN, REPRESENTED BY BOARD;AKOUOS, INC.
发明人:
SIMONS, EMMANUEL JOHN,REISINGER, ELLEN
申请号:
CA3034527
公开号:
CA3034527A1
申请日:
2017.08.23
申请国别(地区):
CA
年份:
2018
代理人:
摘要:
Provided herein are compositions that include at least two different nucleic acid vectors, where each of the at least two different vectors includes a coding sequence that encodes a different portion of an otoferlin protein, and the use of these compositions to treat hearing loss in a subject.