VETOR GÉNICO

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专利权人:

OSPEDALE SAN RAFFAELE S.R.L.;FONDAZIONE TELETHON

发明人:

申请号：

PT10723305

公开号：

PT2424571T

申请日:

2010.04.30

申请国别(地区):

PT

年份:

2020

代理人:

摘要：

A gene vector for use in gene therapy comprising at least one miRNA sequence target operably linked to a nucleotide sequence having a corresponding miRNA in a hematopoietic progenitor cell (HSPC) or hematopoietic stem cell (HSC) which prevents or reduces expression of the nucleotide sequence in a HSPC or HSC but not in a differentiated cell.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/