METHODS AND COMPOSITIONS FOR THE TREATMENT OF FABRY DISEASE

• 收藏
• 分享

专利权人:

Sangamo Therapeutics; Inc.

发明人:

Marshall W. Huston

申请号：

US16734271

公开号：

US20200239911A1

申请日:

2020.01.03

申请国别(地区):

US

年份:

2020

代理人:

摘要：

The present disclosure provides expression constructs comprising a GLA transgene encoding the at least one α-Gal A protein for use in expressing α-Gal A proteins and preventing, inhibiting or treating Fabry disease or one or more symptoms associated with Fabry disease.

来源网站：

中国工程科技知识中心

来源网址：

http://www.ckcest.cn/home/